The Center for Neurologic Study, a nonprofit 501C3 corporation, is a leader in an area now referred to as Translational Medicine. Recently, our director, along with colleagues, were awarded the international Healey Prize for their drug discovery efforts. This was based on the development of antisense molecules (ASOs) that represent a major opportunity to treat heritable diseases of the nervous system, such as familial amyotrophic lateral sclerosis and Huntington’s disease. Further, we are pleased to announce the publication of Neurotherapeutics in the Era of Translational Medicine, which Dr. Smith co-edited with Clive Svendsen and Brian Kaspar.