Ascidian Therapeutics

Ascidian Therapeutics company information, Employees & Contact Information

Ascidian Therapeutics is redefining the treatment of disease by rewriting RNA. By editing exons at the RNA level, Ascidian therapies enable precise post-transcriptional editing of genes, resulting in full-length, functional proteins at the right levels, in the right cells, at the right time. With active discovery and preclinical programs in ophthalmology, neurological and neuromuscular disorders, and other rare diseases, Ascidian is opening new therapeutic possibilities for patients in need of breakthroughs. For more information, visit www.ascidian-tx.com.
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Clinical trial: ABCA4 Retinopathy, (NCT06445322) - CRISPR Medicine News

Clinical trial: ABCA4 Retinopathy, (NCT06445322) CRISPR Medicine News

Ascidian Therapeutics to Present Preclinical Data for RNA Exon Editor, ACDN-01, Supporting an Open IND for Phase 1/2 Clinical Testing at ASGCT 2024 Annual Meeting - PR Newswire

Ascidian Therapeutics to Present Preclinical Data for RNA Exon Editor, ACDN-01, Supporting an Open IND for Phase 1/2 Clinical Testing at ASGCT 2024 Annual Meeting PR Newswire

Clinical trial: ABCA4 Retinopathy, (NCT06467344) - CRISPR Medicine News

Clinical trial: ABCA4 Retinopathy, (NCT06467344) CRISPR Medicine News

Ascidian Therapeutics Launches to Rewrite RNA - PR Newswire

Ascidian Therapeutics Launches to Rewrite RNA PR Newswire

Gene editing: DNA versus RNA - Drug Discovery News

Gene editing: DNA versus RNA Drug Discovery News

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