Eloxx Pharmaceuticals, Inc. is a clinical-stage biopharmaceutical company developing novel RNA-modulating drug candidates that are designed to treat rare and ultra-rare premature stop codon diseases. Premature stop codons are point mutations that disrupt protein synthesis from messenger RNA. As a consequence, patients with premature stop codon diseases have reduced or eliminated protein production from the mutation bearing allele accounting for some of the most severe phenotypes in these genetic diseases. These premature stop codons have been identified in over 1,800 rare and ultra-rare diseases. Read-through therapeutic development is focused on extending mRNA half-life and increasing protein synthesis by enabling the cytoplasmic ribosome to read through premature stop codons to produce full-length proteins. Eloxx’s lead product candidate, ELX-02, is a small molecule drug candidate designed to restore production of full-length functional proteins. ELX-02 is in the early stages of clinical development focusing on cystic fibrosis and cystinosis. ELX-02 is an investigational drug that has not been approved by any global regulatory body. Eloxx is headquartered in Waltham, MA, with R&D operations in Rehovot, Israel.
Company Details
- Employees
- 13
- Founded
- -
- Address
- 480 Arsenal Way Suite 130, Watertown,massachusetts 02472,united States
- Phone
- +1-781-577-5300
- in****@****rma.com
- Industry
- Biotechnology Research
- NAICS
-
Research and Development in Biotechnology (except Nanobiotechnology)
- Website
- eloxxpharma.com
- HQ
- Watertown, Massachusetts
Eloxx Pharmaceuticals Questions
Eloxx Pharmaceuticals's helpline number is +1-781-577-5300
Eloxx Pharmaceuticals's website is eloxxpharma.com
Eloxx Pharmaceuticals's LinkedIn profile is https://www.linkedin.com/company/eloxx-pharmaceuticals
Eloxx Pharmaceuticals has
13 employees.
View email and phone details for 13
employees at Eloxx Pharmaceuticals.
Eloxx Pharmaceuticals's industry is
Biotechnology Research
Eloxx Pharmaceuticals's top competitors are
Emendo Biotherapeutics,
Elox Employee Experience,
Kadimastem Ltd.,
Brainstorm Cell Therapeutics,
Vertex Pharmaceuticals,
Almirall,
Elox,
Prime Medicine, Inc.,
Sanofi,
Quralis.
Eloxx Pharmaceuticals's support email address is info@eloxxpharma.com
Eloxx Pharmaceuticals's categories are Biotechnology Research
Eloxx Pharmaceuticals's founding year is 2013
