SMA Foundation

The mission of the SMA Foundation is to accelerate the development of a treatment for SMA, the number one genetic killer of infants and toddlers. The SMA Foundation was established in 2003 by Loren Eng and Dinakar Singh, parents of a child with SMA. Today, the SMA Foundation is the leading funder of SMA research worldwide–over $100M has been spent on basic, translational, and clinical research. We have invested more than $30M on developing critical, validated research tools and other drug discovery assets. Our mandate is to ensure that all of the results of our research funding are made readily available to every SMA researcher with minimal cost and obligation. The SMA Foundation operates as a unique blend of non-profit, venture capital, and biotech entities. Our leadership comprises seasoned pharmaceutical, biotech, and finance professionals. Because of our innovative strategy and business model, the SMA Foundation frequently serves as an advisor to government, non-profits, universities, professional societies, and the private sector. One of our most important functions is to broker the exchange of critical information and foster new collaborations/alliances. The SMA Foundation serves as the hub and clearinghouse of information for the diverse universes that are involved in drug development. We connect pharmaceutical companies, biotech, academia, non-profits, clinicians, patients, government/regulators, and the media. The work of the SMA Foundation has been recognized by the national media including: ABC News, Bloomberg Markets, Forbes, Fox News, The New York Times, Nightline, Parents Magazine, and the Today Show.