Highly skilled and technically proficient Scientific Leader in RNA Therapeutics, Rare Diseases, Cystic Fibrosis, Respiratory and Metabolic Therapeutics, Lipid-nanoparticles delivery, Pharmacology, Drug Discovery, Drug Development, Preclinical, Nonclinical, Early Clinical Development, New Target Identification, Neuroscience, Molecular Biology, with proven ability to work in a multidisciplinary environment.Proven experience leading collaborative programs within the RNA Therapeutics for Cystic Fibrosis and other respiratory and metabolic diseases. Strong vision to translate nonclinical research to a successful path for early clinical activities. Team leader in target identification and validation for nucleic acid therapeutics for multiple approaches including liver, respiratory, eye and CNS. Experience in the developmental genetic factors affecting human brain disorders, rodent and non-rodent animal models and tumor suppressor/cancer related genes.Leadership with demonstrated ability to efficiently prioritize a broad range of responsibilities in order to achieve maximum level of operating effectiveness. Highly analytic, team player, research-centric professional with expertise in lab and field research, data analysis and project management. Skilled in establishing and managing external collaborations with nonclinical and clinical CROs and KOLs to ensure the advance of the corporate goals and minimize any cost and timeline impact on programs.Organized, take-charge professional with exceptional follow-through abilities and detail orientation; able to plan and oversee projects from concept to successful conclusion. Accomplished speaker and writer with successful publication of high-impact research articles in international scientific publications, including Cell Reports, Nature Neuroscience, Molecular Therapy, Journal of Neuroscience and PNAS. Co-author of several patents within the RNA therapeutics field.Specialties: RNA Therapeutics, Drug Discovery, Drug Development, Pharmacology, Preclinical, Nonclinical, Early Clinical Development, Rare Diseases, Lipid-nanoparticle-based delivery, Cystic Fibrosis, Lung, Liver, CNS, Target Identification and Optimization, Program Lead, Neuroscience, Neurodevelopmental Disorders, Neuroanatomy, Developmental Neurobiology, Brain Development, Rodent/Nonrodent Models, Team Management, Organization Skills, Sequence Optimization and Design, Scientific Writing, Written Communication, Patient Advocacy, Public Speaking, Interpersonal Skills, Mentoring and Management, Molecular Biology, Mouse Genetics.